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Your search for “gene therapy” returned 759 results

UC San Diego Health Joins National Clinical Trial on Hemophilia B Gene Therapy

The Hemophilia and Thrombosis Treatment Center at UC San Diego Health has joined a nationwide clinical trial testing a potential gene therapy that may one day provide a better and long-lasting treatment for people with hemophilia B.

Personalized Medicine Leads to Better Outcomes for Patients with Cancer

…using precision medicine, which emphasizes the use of individual genetics to refine cancer treatment, showed improved response and longer periods of disease remission, even in phase I trials.

A Target for Potential Cancer Drugs May, In Fact, Worsen Disease

Researchers reveal a previously unrealized complexity in cancer development, one that raises concerns and caution about targeting an enzyme popular in oncological treatments.

Underappreciated Protein Plays Critical Role In RNA Regulation and Male Fertility

A protein once thought to be of little consequence has been found to be a central player in processes ranging from male fertility to early embryonic development, according to a study published in the March 31 online issue of Cell by researchers at the University of California, San Diego School…

A Potential New Target for Head and Neck Cancer Immunotherapy

UC San Diego researchers have identified a strong association between the product of a gene expressed in most cancers and elevated levels of white blood cells that produce antibodies within tumors, suggesting a new therapeutic target.

New Cancer Immunotherapy Approach Turns Immune Cells into Tiny Anti-Tumor Drug Factories

In lab and mouse experiments, UC San Diego School of Medicine researchers developed a method to leverage B cells to manufacture and secrete tumor-suppressing microRNAs.

$6.4 Million Grant Funds Glaucoma Study in African-Americans

…of the National Institutes of Health, to elucidate the genetics of glaucoma in persons of African descent.

A World Without Color – Researchers Find Gene Mutation That Strips Color, Reduces Vision

…San Diego Health System have identified a previously unknown gene mutation that underlies this disorder.

Epigenetic Driver of Glioblastoma Provides New Therapeutic Target

Using human tumor samples and mouse models, researchers at University of California, San Diego School of Medicine and Moores Cancer Center discovered that cancer stem cell properties are determined by epigenetic changes — chemical modifications cells use to control which genes are turned on or off.

Drug Targets Hard-to-Reach Leukemia Stem Cells Responsible for Relapses

Researchers at the University of California, San Diego School of Medicine have discovered that hard-to-reach, drug-resistant leukemia stem cells (LSCs) that overexpress multiple pro-survival protein forms are sensitive – and thus vulnerable – to a novel cancer stem cell-targeting drug currently under development.