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Your search for “gene therapy” returned 759 results

Fail-Safe System May Lead to Cures for Inherited Disorders

September 15, 2011

Scientists at the University of California, San Diego School of Medicine have uncovered a previously unknown fail-safe (compensatory) pathway that potentially protects the brain and other organs from genetic and environmental threats.

Multiple Models Reveal New Genetic Links in Autism

November 11, 2014

With the help of mouse models, induced pluripotent stem cells (iPSCs) and the “tooth fairy,” researchers at the University of California, San Diego School of Medicine have implicated a new gene in idiopathic or non-syndromic autism.

New Biomarkers Might Help Personalize Metastatic Colorectal Cancer Treatment

June 17, 2015

…of metastatic colorectal cancer patients. The results revealed two genes that could help physicians make more informed treatment decisions for patients with this disease.

Genetic Changes in Head and Neck Cancer, Immunotherapy Resistance Identified

April 26, 2021

A multi-institutional team of researchers, led by UC San Diego School of Medicine and Moores Cancer Center, has identified both the genetic abnormalities that drive pre-cancer cells into becoming an invasive type of head and neck cancer and patients who are least likely to respond to immunotherapy.

Signaling Molecule Crucial to Stem Cell Reprogramming

November 20, 2014

While investigating a rare genetic disorder, researchers at the University of California, San Diego School of Medicine have discovered that a ubiquitous signaling molecule is crucial to cellular reprogramming, a finding with significant implications for stem cell-based regenerative medicine, wound repair therapies and potential cancer treatments.

UC San Diego Health System Named Center of Excellence for Huntington’s Disease

May 26, 2015

The Huntington’s Disease Clinical Research Center (HDCRC) at UC San Diego Health System has been designated a Center of Excellence by the Huntington’s Disease Society of America (HDSA). UC San Diego was one of only 29 centers nationwide to receive this prestigious designation, which recognizes centers for their elite multidisciplinary…

CIRM Approves $5.8 Million Grant for CAR-T Therapy that Targets Cancer Stem Cells

July 20, 2017

…cancer stem cells, whose survival abilities often render standard therapies ineffective or short-term.

An Errant Editing Enzyme Promotes Tumor Suppressor Loss and Leukemia Propagation

January 3, 2019

UC San Diego researchers have found a stem cell enzyme copy edits more than 20 tumor types, providing new therapeutic target for preventing cancer cell resistance to chemotherapy and radiation.

Albert La Spada Receives Harrington Scholar Award to Combat Neurodegenerative Disease

September 21, 2015

…Harrington Scholar award to advance his work on a therapy for Spinocerebellar ataxia type 7 (SCA7), a rare but devastating neurological disorder that can lead to blindness and progressive loss of physical coordination.

Poseidon Innovation Announces Funding for Three UC San Diego Researchers

June 26, 2020

UC San Diego and Deerfield Management created Poseidon Innovation to support researchers working to advance disease-curing therapeutics by funding early stage projects and expediting the drug-development cycle. Poseidon announces it is funding three researchers.

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