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Your search for “gene therapy” returned 759 results

Spotlight on Faculty Research: Stem Cell

November 14, 2011

…cells aimed at developing therapies for heart failure and cardiac pacemaker dysfunction. To repair of human heart, it is important to study human cardiac progenitors and to define pathways required to grow and differentiate them utilizing human cells as a model experimental system. Evans’ lab will create special lines of…

Discovery Could Lead to Novel Therapies for Fragile X Syndrome

April 17, 2014

Scientists studying the most common form of inherited mental disability—a genetic disease called “Fragile X syndrome”—have uncovered new details about the cellular processes responsible for the condition that could lead to the development of therapies to restore some of the capabilities lost in affected individuals.

CAR Trials Drive Leukemia and Lymphoma Treatment in New Direction

February 23, 2016

…different types of blood cancer that often defy existing therapies.

Gene Networks for Innate Immunity Linked to PTSD Risk

March 10, 2015

…in New York and the United Kingdom, have identified genetic markers, derived from blood samples that are linked to post-traumatic stress disorder (PTSD). The markers are associated with gene networks that regulate innate immune function and interferon signaling.

Human Brain Cell Atlas Offers Unprecedented Look at Neuropsychiatric Disorders

October 13, 2023

In a large, multi-institutional effort led by University of California San Diego, researchers have analyzed more than a million human brain cells and revealed links between specific types of cells and various common neuropsychiatric disorders.

UC San Diego Health is First in San Diego to offer CAR T-cell Therapy for Some Cancers

December 3, 2018

Following the FDA’s approval of chimeric antigen receptor (CAR) T-cell therapies for the treatment of certain types of non-Hodgkin lymphomas, UC San Diego Health was the first medical center in San Diego to be certified to offer this type of immunotherapy outside of a clinical trial.

Body’s Own Gene Editing System Generates Leukemia Stem Cells

June 9, 2016

Cancer stem cells are like zombies — even after a tumor is destroyed, they can keep coming back. These cells have an unlimited capacity to regenerate themselves, making more cancer stem cells and more tumors. Researchers at University of California San Diego School of Medicine have now unraveled how pre-leukemic…

Don Cleveland Wins a Trifecta of Recognition

January 31, 2023

In the span of just a few weeks, Don Cleveland, a leading researcher in the study of neurodegenerative diseases like ALS and Alzheimer’s, has received three major awards.

Phase I Trial Finds Experimental Drug Safe in Treating Chronic Lymphocytic Leukemia

June 1, 2018

Reporting results from a first-in-human phase I clinical trial, researchers at University of California San Diego School of Medicine have found that treatment with cirmtuzumab, an experimental monoclonal antibody-based drug, measurably inhibited the “stemness” of chronic lymphocytic leukemia cancer (CLL) cells — their ability to self-renew and resist terminal differentiation…

A Better Way to Track Emerging Cell Therapies Using MRIs

September 19, 2014

Researchers at the University of California, San Diego School of Medicine, University of Pittsburgh and elsewhere describe the first human tests of using a perfluorocarbon (PFC) tracer in combination with non-invasive magnetic resonance imaging (MRI) to track therapeutic immune cells injected into patients with colorectal cancer.

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