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Your search for “gene therapy” returned 50 results

Scientists Receive $4.8M to Pursue Gene Therapy for ‘Incurable’ Disease

The California Institute for Regenerative Medicine has awarded UC San Diego researchers $4.8 million to advance a gene therapy to treat Friedreich’s ataxia, a rare but devastating neuromuscular disorder.

How Gene Therapy May Hold Key to Treating Life-Threatening Cardiac Disease

New study finds gene therapy improved cardiac, muscle and liver function in Danon disease mouse models.

Gene Therapy Finds New Life in an Old Home

An international symposium November 17-18, 2022 at UC San Diego will discuss current clinical trials using gene therapy, here and abroad.

Southern California’s First Real-Time MRI-Guided Gene Therapy for Brain Cancer

Neurosurgeons at the University of California, San Diego School of Medicine and UC San Diego Moores Cancer Center are among the first in the world to utilize real-time magnetic resonance imaging (MRI) guidance for delivery of gene therapy as a potential treatment for brain tumors.

Friedmann Recognized for Pioneering Gene Therapy Research

Friedman Recognized for Pioneering Gene Therapy Research School of Medicine professor receives prestigious Japan Prize Theodore Friedmann Theodore Friedmann, MD, professor in the Department of Pediatrics at University of California, San Diego School of Medicine was named today one of three recipients of the 2015 Japan Prize, a prestigious international…

Gene Therapy in Alzheimer’s Disease Mouse Model Preserves Learning and Memory

Researchers at UC San Diego have used gene therapy to prevent learning and memory loss in a mouse model of Alzheimer’s disease, a key step toward eventually testing the approach in humans with the neurodegenerative disease.

Degenerating Neurons Respond to Gene Therapy Treatment for Alzheimer’s Disease

Degenerating neurons in patients with Alzheimer’s disease (AD) measurably responded to an experimental gene therapy in which nerve growth factor (NGF) was injected into their brains, report researchers at University of California, San Diego School of Medicine in the current issue of JAMA Neurology.

Gene Therapy Approach Shows Promise in Treating ALS

Researchers report that a gene therapy approach, developed at UC San Diego measurably delayed disease onset in humanized mouse and rat models of familial ALS, an inherited form of the disease that runs in families.

First-in-Human Clinical Trial to Assess Gene Therapy for Alzheimer’s Disease

UC San Diego researchers have launched a first-in-human Phase I clinical trial to assess the safety and efficacy of a gene therapy to deliver a key protein into the brains of persons with Alzheimer’s disease or Mild Cognitive Impairment, a condition that often precedes full-blown dementia.

Friedmann Named 2015 Japan Prize Winner

Theodore Friedmann, MD, professor in the Department of Pediatrics at University of California, San Diego School of Medicine was named today one of three recipients of the 2015 Japan Prize, a prestigious international award honoring laureates whose “original and outstanding achievements in science and technology have advanced the frontiers of…