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Your search for “gene therapy” returned 735 results

UC San Diego Launches Gene Therapy Initiative, Targeting Treatments for Rare Diseases

August 29, 2023

A $5 million gift from the Nancy and Geoffrey Stack Foundation has established the UC San Diego Gene Therapy Initiative to find novel therapies for children and adults with genetic diseases.

Researchers ID Cancer Gene-Drug Combinations Ripe for Precision Medicine

July 21, 2016

…the number of cancer gene mutations that can be specifically targeted with personalized therapies, researchers at University of California San Diego School of Medicine and Moores Cancer Center looked for combinations of mutated genes and drugs that together kill cancer cells. The study, published July 21 in Molecular Cell, uncovered…

How Gene Therapy May Hold Key to Treating Life-Threatening Cardiac Disease

March 18, 2020

New study finds gene therapy improved cardiac, muscle and liver function in Danon disease mouse models.

UC San Diego Awarded $8M to Expand Stem Cell Therapy Clinical Trials

November 21, 2022

UC San Diego Alpha Stem Cell Clinic awarded $8M to expand clinical trials of novel stem cell therapies. The CIRM award will advance partnerships between academic and industry experts in San Diego to expedite clinical trials for patients with difficult-to-treat diseases.

Promise of Gene Therapy for Glaucoma Shines Bright in Award-Winning Image

October 17, 2016

Whether you see the gossamer wings of a butterfly or the delicate opened petals of a flower, there is beauty in the eye of the beholder — a mouse retina described and visually captured by scientists at the National Center for Microscopy and Imaging Research (NCMIR) at University of California…

SDSC/UCSD Study Uncovers Mechanisms of Cancer-Causing Mutations

March 18, 2015

Researchers at the San Diego Supercomputer Center (SDSC) and the Moores Cancer Center at the University of California, San Diego, have described for the first time the molecular mechanism of cancer development caused by well-known “resistance” mutations in the gene called epidermal growth factor receptor (EGFR).

How Loss of Single Gene Fuels Deadly Childhood Brain Cancer

September 10, 2020

UC San Diego researchers describe how the functional loss of a single gene negatively impacts neural development and promotes the growth of a particularly deadly form of pediatric brain cancer.

UC San Diego/SDSC Study Advances Brain Cancer Research

February 11, 2015

Researchers at the San Diego Supercomputer Center (SDSC), Moores Cancer Center, and Department of Neurosciences at the University of California, San Diego, have shown for the first time a pyramid hierarchical network of “coherent gene modules” that regulate glioblastoma genes, involved in a highly aggressive form of brain cancer.

Friedmann Recognized for Pioneering Gene Therapy Research

January 29, 2015

Friedman Recognized for Pioneering Gene Therapy Research School of Medicine professor receives prestigious Japan Prize Theodore Friedmann Theodore Friedmann, MD, professor in the Department of Pediatrics at University of California, San Diego School of Medicine was named today one of three recipients of the 2015 Japan Prize, a prestigious international…

Proposed Drug May Reverse Huntington’s Disease Symptoms

June 20, 2012

With a single drug treatment, researchers at the Ludwig Institute for Cancer Research at the University of California, San Diego School of Medicine can silence the mutated gene responsible for Huntington’s disease, slowing and partially reversing progression of the fatal neurodegenerative disorder in animal models.

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