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Your search for “Gene Therapy” returned 776 results

UC San Diego Health Offers Novel Gene Therapy for Bladder Cancer

July 8, 2024

UC San Diego Health is the first health system in San Diego County to offer novel gene therapy for bladder cancer.

Scientists Receive $4.8M to Pursue Gene Therapy for ‘Incurable’ Disease

December 1, 2022

The California Institute for Regenerative Medicine has awarded UC San Diego researchers $4.8 million to advance a gene therapy to treat Friedreich’s ataxia, a rare but devastating neuromuscular disorder.

Friedmann Named 2015 Japan Prize Winner

January 28, 2015

Theodore Friedmann, MD, professor in the Department of Pediatrics at University of California, San Diego School of Medicine was named today one of three recipients of the 2015 Japan Prize, a prestigious international award honoring laureates whose “original and outstanding achievements in science and technology have advanced the frontiers of…

Altered Cell Cycle Gene Activity Underlies Brain Overgrowth in Autistic Toddlers

December 14, 2015

Further underscoring the prenatal origins of Autism Spectrum Disorder (ASD), researchers at University of California, San Diego School of Medicine describe for the first time how abnormal gene activity in cell cycle networks that are known to control brain cell production may underlie abnormal early brain growth in the disorder.

New Research Helps Explain the Genetic Basis of Why We Look the Way We Do

November 10, 2021

Comparing features of a common laboratory fruit fly with its rarer cousin collected from Hawai’i Volcanoes National Park, UC San Diego researchers used CRISPR technology to uncover clues about how high-level control genes called Hox genes shape our appearance.

“Soft” CRISPR May Offer a New Fix for Genetic Defects

July 1, 2022

Scientists have developed a CRISPR-based technology that could offer a safer approach to correcting genetic defects. The new “soft” CRISPR system makes use of natural DNA repair machinery, providing a foundation for novel gene therapy strategies with the potential to cure genetic diseases.

Personalized “Eye-in-a-Dish” Models Reveal Genetic Underpinnings of Macular Degeneration

May 9, 2019

Using stem cells derived from six people, UC San Diego School of Medicine researchers recapitulated retinal cells in the lab. This “eye-in-a-dish” model allowed them to identify genetic variants that cause age-related macular degeneration, a common cause of vision loss.

With Gene Therapy, Scientists Develop Opioid-Free Solution for Chronic Pain

March 10, 2021

A gene therapy for chronic pain could offer a safer, non-addictive alternative to opioids. By temporarily repressing a gene involved in sensing pain, the treatment increased pain tolerance in mice, lowered their sensitivity to pain and provided months of pain relief without causing numbness.

Gene Editing Technique Helps Find Cancer’s Weak Spots

March 20, 2017

Genetic mutations that cause cancer also weaken cancer cells, allowing researchers to develop drugs that will selectively kill them. This is called “synthetic lethality” because the drug is only lethal to mutated (synthetic) cells. Researchers at UC San Diego School of Medicine and Jacobs School of Engineering developed a method…

‘Care Fair for Gender Affirmation’ Hosted by Interdisciplinary Student Health and Wellbeing Team

April 11, 2023

UC San Diego’s Student Health Services (SHS) has launched a new Interdisciplinary Gender-Affirming Care Team as part of the Student Health and Wellbeing (SHW) cluster. Students who are exploring their gender identity are invited to attend the upcoming Care Fair on April 11.

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